LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD)
Clinical trials for LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD) explained in plain language.
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Breakthrough oil trial aims to protect kids from metabolic crises
Disease control OngoingThis study is testing whether a special nutritional oil called triheptanoin can reduce serious health events like muscle breakdown, heart problems, and low blood sugar in children with a rare disorder where their bodies struggle to use fats for energy. About 69 children under 18 …
Matched conditions: LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD)
Phase: PHASE3 • Sponsor: Ultragenyx Pharmaceutical Inc • Aim: Disease control
Last updated Mar 30, 2026 14:30 UTC
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Decade-Long watch: tracking a rare Disease's impact on families
Knowledge-focused OngoingThis study aims to collect long-term safety and health information from up to 150 children and adults with a rare metabolic disorder called LC-FAOD. It will follow participants for up to 10 years to understand the natural course of the disease and monitor the safety of a specific…
Matched conditions: LONG-CHAIN FATTY ACID OXIDATION DISORDERS (LC-FAOD)
Sponsor: Ultragenyx Pharmaceutical Inc • Aim: Knowledge-focused
Last updated Mar 25, 2026 14:08 UTC