New oil therapy could slash Life-Threatening events in kids with rare metabolic disease
NCT ID NCT05933200
First seen Jun 27, 2026 · Last updated Jul 22, 2026 · Updated 2 times
Summary
This study tests whether triheptanoin, a special oil, can reduce major clinical events (like severe low blood sugar or heart problems) in children with long-chain fatty acid oxidation disorders (LC-FAOD), a rare condition where the body can't break down certain fats for energy. About 69 kids under 18 will receive either triheptanoin or a standard MCT oil, and researchers will track how often serious events occur over time. The goal is to see if triheptanoin offers better disease control than current treatments.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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Cerrahpasa Medical Faculty
Istanbul, 34116, Turkey (Türkiye)
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Cukurova University
Adana, Turkey (Türkiye)
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Ege University
Bornova-İzmir, Turkey (Türkiye)
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Gazi University
Ankara, Turkey (Türkiye)
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Gdańksi Uniwersytet Medyczny
Gdansk, Pomeranian Voivodeship, 80-952, Poland
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General University Hospital in Prague-GUH (Všeobecná fakultní nemocnice v Praze- VFN)
Prague, 120-08, Czechia
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Instytut Pomnik-Centrum Zdrowia Dziecka
Warsaw, Masovian Voivodeship, 04-730, Poland
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Istanbul Universitesi Istanbul Tip Fakultesi Hastanesi
Istanbul, 34093, Turkey (Türkiye)
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Juntendo University Hospital
Bunkyo City, Tokyo, 113-8431, Japan
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King Faisal Specialist Hospital & Research Centre
Riyadh, 11211, Saudi Arabia
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Sant Joan de Deu Hospital (SJD)
Barcelona, Esplugues de Llobregat, 08950, Spain
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The Jikei University Hospital
Minato, Tokyo, Japan
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University Hospital 12 de Octubre
Madrid, 28041, Spain
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University Hospital Santiago de Compostela
A Coruña, 15706, Spain
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Universitätsklinikum Freiburg
Freiburg im Breisgau, 79106, Germany
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