LATE-ONSET POMPE DISEASE

Clinical trials for LATE-ONSET POMPE DISEASE explained in plain language.

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Not yet recruiting 1 Not yet finished but already full! 1 Completed 1

First patients test new genetic drug for rare muscle disease

Disease control Ongoing

This is the first human study testing ABX1100, a new drug for late-onset Pompe disease—a rare genetic disorder that weakens muscles. Researchers will check the safety of different doses in 46 healthy volunteers and patients with the disease. The study will measure how the drug mo…

Matched conditions: LATE-ONSET POMPE DISEASE

Phase: EARLY_PHASE1 • Sponsor: Aro Biotherapeutics • Aim: Disease control

Last updated Mar 23, 2026 15:15 UTC

LATE-ONSET POMPE DISEASE

Get alerted when new LATE-ONSET POMPE DISEASE trials appear

First patients test new genetic drug for rare muscle disease