LATE-ONSET POMPE DISEASE
Clinical trials for LATE-ONSET POMPE DISEASE explained in plain language.
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New pompe disease drug moves to first human tests
Disease control CompletedThis early-phase study tested a new drug called ABX1100 in 46 people, including healthy volunteers and patients with late-onset Pompe disease. The main goal was to check safety and how the drug moves through the body. Researchers gave single or multiple doses to find the right am…
Matched conditions: LATE-ONSET POMPE DISEASE
Phase: EARLY_PHASE1 • Sponsor: Aro Biotherapeutics • Aim: Disease control
Last updated Jun 27, 2026 12:30 UTC
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Home breathing training shows promise for pompe patients
Symptom relief CompletedThis study tested whether high-dose inspiratory muscle training (IMT) using a handheld device is safe and feasible for people with late-onset Pompe disease. 34 adults with stable Pompe disease did remote breathing exercises. Researchers measured changes in respiratory strength an…
Matched conditions: LATE-ONSET POMPE DISEASE
Phase: NA • Sponsor: Duke University • Aim: Symptom relief
Last updated Jun 27, 2026 07:53 UTC
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Pompe disease may raise risk of brain aneurysms, new study investigates
Knowledge-focused CompletedThis study investigates whether people with late-onset Pompe disease have a higher risk of severe blood vessel problems in the brain and aorta. Researchers will collect medical and genetic data from adults with Pompe disease and from those who have had a brain aneurysm or bleedin…
Matched conditions: LATE-ONSET POMPE DISEASE
Sponsor: Hospitales Universitarios Virgen del Rocío • Aim: Knowledge-focused
Last updated Jul 08, 2026 00:00 UTC