HUNTINGTON'S DISEASE

Clinical trials for HUNTINGTON'S DISEASE explained in plain language.

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Trials to join now! 5 Not yet finished but already full! 1 Completed 1 Terminated 1

Brain-Injected gene therapy aims to halt devastating Huntington's disease

Disease control Ongoing

This early-stage trial is testing a one-time gene therapy called AMT-130, which is injected directly into the brain. The goal is to see if lowering the harmful huntingtin protein is safe and can slow the progression of Huntington's disease in 43 people with early symptoms. The st…

Matched conditions: HUNTINGTON'S DISEASE

Phase: PHASE1, PHASE2 • Sponsor: UniQure Biopharma B.V. • Aim: Disease control

Last updated Apr 01, 2026 14:41 UTC

HUNTINGTON'S DISEASE

Get alerted when new HUNTINGTON'S DISEASE trials appear

Brain-Injected gene therapy aims to halt devastating Huntington's disease