HEMOPHILIA A
Clinical trials for HEMOPHILIA A explained in plain language.
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Gene therapy trial seeks to free hemophilia patients from frequent injections
Disease control Not yet recruitingThis early-stage study is testing the safety of an experimental gene therapy called SPK-8011QQ in adult men with severe hemophilia A. The main goal is to see if the treatment is safe and well-tolerated, not to prove it works. Researchers will carefully monitor five participants f…
Matched conditions: HEMOPHILIA A
Phase: PHASE1, PHASE2 • Sponsor: Hoffmann-La Roche • Aim: Disease control
Last updated Apr 01, 2026 14:40 UTC
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New hemophilia Drug's impact on Kids' joints under investigation
Disease control Not yet recruitingThis study aims to understand how emicizumab, a newer subcutaneous treatment for Hemophilia A, affects the musculoskeletal system in children. Researchers will measure joint health, pain levels, mobility, and quality of life in 20 children under 18 with severe Hemophilia A (facto…
Matched conditions: HEMOPHILIA A
Sponsor: Hasan Kalyoncu University • Aim: Disease control
Last updated Mar 30, 2026 14:34 UTC
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New hemophilia drug aims to outperform current standard
Disease control Not yet recruitingThis study is testing whether a new preventive drug called NXT007 works better than the current standard treatment, emicizumab, at reducing bleeding episodes in people with hemophilia A. It will involve 360 participants aged 12 and older who have moderate to severe hemophilia, wi…
Matched conditions: HEMOPHILIA A
Phase: PHASE3 • Sponsor: Hoffmann-La Roche • Aim: Disease control
Last updated Mar 30, 2026 14:34 UTC
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New hemophilia drug aims to outperform standard therapy in major trial
Disease control Not yet recruitingThis study aims to see if a new preventive treatment called NXT007 works better and is as safe as the current standard factor VIII injections for people with moderate or severe hemophilia A. It will involve about 126 people aged 12 and older who are already using factor VIII to p…
Matched conditions: HEMOPHILIA A
Phase: PHASE3 • Sponsor: Hoffmann-La Roche • Aim: Disease control
Last updated Mar 19, 2026 14:56 UTC
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Tracking real-world results of a bleeding disorder drug in kids
Knowledge-focused Not yet recruitingThis study aims to learn more about how well an already-approved hemophilia A treatment works for children during their regular medical care. Researchers will collect information from about 40 children aged 7 to 12 who are already taking the drug damoctocog alfa pegol to prevent …
Matched conditions: HEMOPHILIA A
Sponsor: Bayer • Aim: Knowledge-focused
Last updated Apr 01, 2026 14:43 UTC
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Scientists seek liver clues years after hemophilia gene therapy
Knowledge-focused Not yet recruitingThis study aims to understand the long-term effects of gene therapy on the liver in adults with hemophilia. Researchers will analyze small liver tissue samples from up to 8 people who received gene therapy at least 6 months ago. The goal is to see how the liver cells have respond…
Matched conditions: HEMOPHILIA A
Sponsor: St. Jude Children's Research Hospital • Aim: Knowledge-focused
Last updated Mar 23, 2026 15:14 UTC