GLYCOGEN STORAGE DISEASE TYPE II

Clinical trials for GLYCOGEN STORAGE DISEASE TYPE II explained in plain language.

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Trials to join now! 2 Not yet finished but already full! 1

French patients continue Life-Changing pompe treatment in Long-Term safety study

Disease control Ongoing

This study provides continued access to enzyme replacement therapy for French patients with Pompe disease who completed earlier research trials. It follows 17 patients for approximately four years to monitor long-term safety and track how well the treatment maintains their walkin…

Matched conditions: GLYCOGEN STORAGE DISEASE TYPE II

Phase: PHASE4 • Sponsor: Genzyme, a Sanofi Company • Aim: Disease control

Last updated Mar 19, 2026 14:56 UTC

GLYCOGEN STORAGE DISEASE TYPE II

Get alerted when new GLYCOGEN STORAGE DISEASE TYPE II trials appear

French patients continue Life-Changing pompe treatment in Long-Term safety study