GAUCHER DISEASE TYPE 1

Clinical trials for GAUCHER DISEASE TYPE 1 explained in plain language.

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Trials to join now! 2 Not yet recruiting 1 Not yet finished but already full! 1 Completed 2

One-Shot gene therapy could end lifelong injections for gaucher disease

⭐️ CURE ⭐️ Not yet recruiting

This study is testing a one-time gene therapy called FLT201 for adults with Gaucher disease type 1. The goal is to see if this single treatment can replace the need for lifelong, regular enzyme replacement therapy. Researchers will check if the therapy is safe and if it keeps pat…

Matched conditions: GAUCHER DISEASE TYPE 1

Phase: PHASE3 • Sponsor: Spur Therapeutics • Aim: ⭐️ CURE ⭐️

Last updated Mar 23, 2026 15:15 UTC

GAUCHER DISEASE TYPE 1

Get alerted when new GAUCHER DISEASE TYPE 1 trials appear

One-Shot gene therapy could end lifelong injections for gaucher disease