GAUCHER DISEASE TYPE 1

Clinical trials for GAUCHER DISEASE TYPE 1 explained in plain language.

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Trials to join now! 2 Not yet recruiting 1 Not yet finished but already full! 1 Completed 2

Scientists track patients for 5 years after pioneering gene therapy

Disease control Ongoing

This study is following 75 adults with Gaucher disease type 1 for five years after they received an experimental gene therapy called FLT201. The main goal is to monitor their long-term safety and see how well the treatment's effects last over time. It is a follow-up to an earlier…

Matched conditions: GAUCHER DISEASE TYPE 1

Phase: PHASE1, PHASE2 • Sponsor: Spur Therapeutics • Aim: Disease control

Last updated Mar 10, 2026 12:52 UTC

GAUCHER DISEASE TYPE 1

Get alerted when new GAUCHER DISEASE TYPE 1 trials appear

Scientists track patients for 5 years after pioneering gene therapy