FRIEDREICH ATAXIA
Clinical trials for FRIEDREICH ATAXIA explained in plain language.
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Early trial tests drug to save sight in rare neurological disease
Disease control CompletedThis small, completed pilot study tested whether a drug called elamipretide is safe and might help control vision loss in people with advanced Friedreich ataxia (FRDA). Twenty participants with FRDA-related vision or heart problems received either a low or high dose of the drug f…
Matched conditions: FRIEDREICH ATAXIA
Phase: PHASE1, PHASE2 • Sponsor: Children's Hospital of Philadelphia • Aim: Disease control
Last updated Mar 23, 2026 15:16 UTC
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New drug shows promise for slowing rare neurological disease
Disease control CompletedThis study tested a drug called omaveloxolone (RTA 408) to see if it could help people with Friedreich's ataxia, a rare genetic disease that affects movement and coordination. Researchers enrolled 172 participants to measure the drug's safety and its effects on physical effort an…
Matched conditions: FRIEDREICH ATAXIA
Phase: PHASE2 • Sponsor: Biogen • Aim: Disease control
Last updated Mar 23, 2026 15:14 UTC
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Can simple breathing exercises help a rare nerve disease?
Symptom relief CompletedThis study tested whether a 12-week program of breathing exercises could help people with Friedreich's ataxia swallow more safely and breathe better. Researchers measured lung strength and swallowing ability before and after the training in one participant. The goal was to see if…
Matched conditions: FRIEDREICH ATAXIA
Phase: NA • Sponsor: University of Florida • Aim: Symptom relief
Last updated Mar 30, 2026 14:29 UTC
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Scientists search for a new tool to track a rare neurological disease
Knowledge-focused CompletedThis study aimed to find a new way to measure a specific biological signal (frataxin mRNA) in the blood and spinal fluid of people with Friedreich's ataxia. Researchers tested 10 adult patients to see if this measurement could serve as a useful tool to track the disease and monit…
Matched conditions: FRIEDREICH ATAXIA
Sponsor: University of Florida • Aim: Knowledge-focused
Last updated Mar 30, 2026 14:35 UTC