FAMILIAL PLATELET DISORDER

Clinical trials for FAMILIAL PLATELET DISORDER explained in plain language.

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Trials to join now! 1

New hope for controlling a rare blood disorder that raises cancer risk

Disease control Recruiting now

This study is testing if a low dose of the drug sirolimus is safe and can improve blood cell production in adults with RUNX1 familial platelet disorder. This inherited condition causes low platelets, easy bleeding, and a high risk of blood cancers. Researchers will see if the dru…

Matched conditions: FAMILIAL PLATELET DISORDER

Phase: PHASE2 • Sponsor: M.D. Anderson Cancer Center • Aim: Disease control

Last updated Mar 30, 2026 14:29 UTC

FAMILIAL PLATELET DISORDER

Get alerted when new FAMILIAL PLATELET DISORDER trials appear

New hope for controlling a rare blood disorder that raises cancer risk