FABRY DISEASE
Clinical trials for FABRY DISEASE explained in plain language.
Never miss a new study
Get alerted when new FABRY DISEASE trials appear
Sign up with your email to follow new studies for FABRY DISEASE, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Real-World tracking begins for rare disease treatment
Disease control Not yet recruitingThis study aims to collect long-term information on how well and how safely a medication called pegunigalsidase alfa works for adults with Fabry disease. It will follow about 75 patients who are already taking or planning to start this treatment in their normal healthcare setting…
Matched conditions: FABRY DISEASE
Sponsor: Chiesi Italia • Aim: Disease control
Last updated Mar 23, 2026 15:15 UTC
-
Scientists hunt for hidden clues in fabry disease hearts
Knowledge-focused Not yet recruitingThis study aims to find new ways to detect and predict heart problems in people with Fabry disease. Researchers will use special heart scans and analyze tiny molecules in blood and tissue samples from about 20 adult patients. The goal is to better understand how the disease damag…
Matched conditions: FABRY DISEASE
Sponsor: Núcleo de Apoio à Investigação Clínica - FMUP • Aim: Knowledge-focused
Last updated Mar 31, 2026 12:12 UTC