CONGENITAL SIDEROBLASTIC ANEMIA

Clinical trials for CONGENITAL SIDEROBLASTIC ANEMIA explained in plain language.

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New transplant approach may help kids with rare bone marrow diseases

Disease control Ongoing

This study tests a milder chemotherapy regimen (fludarabine-based) before a bone marrow transplant from a matched sibling donor. It includes up to 25 children and young adults (ages 0-22) with acquired aplastic anemia or inherited bone marrow failure. The goal is to see if this a…

Matched conditions: CONGENITAL SIDEROBLASTIC ANEMIA

Phase: EARLY_PHASE1 • Sponsor: Children's Hospital of Philadelphia • Aim: Disease control

Last updated Jun 17, 2026 06:54 UTC

CONGENITAL SIDEROBLASTIC ANEMIA

Get alerted when new CONGENITAL SIDEROBLASTIC ANEMIA trials appear

New transplant approach may help kids with rare bone marrow diseases