New transplant approach may help kids with rare bone marrow diseases
NCT ID NCT02928991
First seen May 31, 2026 · Last updated Jun 16, 2026 · Updated 2 times
Summary
This study tests a milder chemotherapy regimen (fludarabine-based) before a bone marrow transplant from a matched sibling donor. It includes up to 25 children and young adults (ages 0-22) with acquired aplastic anemia or inherited bone marrow failure. The goal is to see if this approach helps the donor cells successfully take hold and reduces transplant-related risks.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
Conditions
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Conditions inferred from the trial description
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