CONGENITAL SIDEROBLASTIC ANEMIA

Clinical trials for CONGENITAL SIDEROBLASTIC ANEMIA explained in plain language.

Never miss a new study

Get alerted when new CONGENITAL SIDEROBLASTIC ANEMIA trials appear

Sign up with your email to follow new studies for CONGENITAL SIDEROBLASTIC ANEMIA, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.

Our safety recommendation!

By submitting, you agree to our Terms of use

Not yet finished but already full! 1

New transplant approach may help kids with rare bone marrow diseases

Disease control Ongoing

This study tests a milder chemotherapy regimen (fludarabine-based) before a bone marrow transplant from a matched sibling donor. It includes up to 25 children and young adults (ages 0-22) with acquired aplastic anemia or inherited bone marrow failure. The goal is to see if this a…

Matched conditions: CONGENITAL SIDEROBLASTIC ANEMIA

Phase: EARLY_PHASE1 • Sponsor: Children's Hospital of Philadelphia • Aim: Disease control

Last updated Jun 17, 2026 05:39 UTC

CONGENITAL SIDEROBLASTIC ANEMIA

Get alerted when new CONGENITAL SIDEROBLASTIC ANEMIA trials appear

New transplant approach may help kids with rare bone marrow diseases