CANAVAN DISEASE
Clinical trials for CANAVAN DISEASE explained in plain language.
Never miss a new study
Get alerted when new CANAVAN DISEASE trials appear
Sign up with your email to follow new studies for CANAVAN DISEASE, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Gene therapy hope for rare brain disease in toddlers
Disease control Recruiting nowThis study tests a gene therapy called BBP-812 for children with Canavan disease, a rare and serious brain disorder. The therapy uses a harmless virus to deliver a working copy of the missing gene. The goal is to see if it is safe and can improve symptoms in up to 26 children und…
Matched conditions: CANAVAN DISEASE
Phase: PHASE1, PHASE2 • Sponsor: Aspa Therapeutics • Aim: Disease control
Last updated May 15, 2026 11:57 UTC
-
Massive leukodystrophy biobank aims to unlock disease secrets
Knowledge-focused Recruiting nowThis study collects medical information and biological samples from up to 12,000 people with leukodystrophies—rare brain disorders affecting white matter. Researchers will use this data to find new genetic causes, develop biomarkers, and better understand how these diseases progr…
Matched conditions: CANAVAN DISEASE
Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated May 13, 2026 16:02 UTC