ATROPHY

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Trials to join now! 1 Not yet finished but already full! 1 Completed 1

Muscle-Boosting drug shows promise for children with rare neuromuscular disease

Disease control Completed

This completed Phase 3 trial tested whether adding the experimental drug apitegromab to standard SMA treatments could improve muscle function in 188 children and young adults (ages 2-21) with later-onset spinal muscular atrophy. All participants were already receiving approved SM…

Matched conditions: ATROPHY

Phase: PHASE3 • Sponsor: Scholar Rock, Inc. • Aim: Disease control

Last updated Mar 30, 2026 14:30 UTC

ATROPHY

Get alerted when new ATROPHY trials appear

Muscle-Boosting drug shows promise for children with rare neuromuscular disease