ALAGILLE SYNDROME
Clinical trials for ALAGILLE SYNDROME explained in plain language.
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New drug livmarli tracked for Long-Term safety in kids with rare liver disorders
Disease control Recruiting nowThis study follows 230 children with Alagille syndrome or progressive familial intrahepatic cholestasis (PFIC) who are taking Livmarli, a drug to reduce bile buildup and itching. Researchers will monitor side effects, liver function, and long-term outcomes like need for transplan…
Matched conditions: ALAGILLE SYNDROME
Phase: PHASE4 • Sponsor: Mirum Pharmaceuticals, Inc. • Aim: Disease control
Last updated Jun 27, 2026 14:02 UTC
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Can a daily pill help kids with rare liver disease avoid transplant?
Disease control Recruiting nowThis study follows 30 people with Alagille syndrome who are taking odevixibat (Bylvay) in their daily lives. The goal is to see if the drug helps them avoid serious surgeries like liver transplant or bile duct repair over the long term. Researchers will also track weight, height,…
Matched conditions: ALAGILLE SYNDROME
Sponsor: Ipsen • Aim: Disease control
Last updated Jun 27, 2026 12:39 UTC
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New hope for kids with rare liver disease: long-term drug study launched
Symptom relief Recruiting nowThis study looks at the long-term safety and effectiveness of odevixibat in 70 people with Alagille syndrome, a rare genetic condition that affects the liver and other organs. The drug aims to reduce severe itching and improve bile flow. Participants who completed a prior 24-week…
Matched conditions: ALAGILLE SYNDROME
Phase: PHASE3 • Sponsor: Albireo, an Ipsen Company • Aim: Symptom relief
Last updated Jun 27, 2026 12:38 UTC