AICARDI GOUTIERES SYNDROME
Clinical trials for AICARDI GOUTIERES SYNDROME explained in plain language.
Never miss a new study
Get alerted when new AICARDI GOUTIERES SYNDROME trials appear
Sign up with your email to follow new studies for AICARDI GOUTIERES SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Could a drug calm the immune attack in aicardi goutières syndrome?
Disease control CompletedThis study tested the drug baricitinib in 54 people with Aicardi Goutières Syndrome (AGS), a rare genetic disorder where the immune system attacks the brain. The goal was to see if the drug could safely slow or stop the disease by reducing harmful inflammation. Researchers measur…
Matched conditions: AICARDI GOUTIERES SYNDROME
Phase: PHASE2 • Sponsor: Adeline Vanderver, MD • Aim: Disease control
Last updated Jun 17, 2026 00:28 UTC
-
Gene sequencing breakthrough offers faster diagnosis for rare brain diseases
Diagnosis CompletedThis study looked at whether whole genome sequencing (a complete read of a person's DNA) can help diagnose leukodystrophies, a group of rare brain disorders affecting white matter, more effectively than standard methods. Researchers enrolled 236 children under 18 with abnormal br…
Matched conditions: AICARDI GOUTIERES SYNDROME
Sponsor: Children's Hospital of Philadelphia • Aim: Diagnosis
Last updated Jun 15, 2026 19:07 UTC