AICARDI GOUTIERES SYNDROME
Clinical trials for AICARDI GOUTIERES SYNDROME explained in plain language.
Never miss a new study
Get alerted when new AICARDI GOUTIERES SYNDROME trials appear
Sign up with your email to follow new studies for AICARDI GOUTIERES SYNDROME, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
Could a rheumatoid arthritis drug calm a rare brain disease?
Disease control CompletedThis phase 2 trial tested baricitinib (Olumiant), a drug used for rheumatoid arthritis, in 54 people with Aicardi Goutières Syndrome (AGS), a rare genetic disorder that causes brain inflammation and developmental problems. The goal was to see if the drug could stabilize or improv…
Matched conditions: AICARDI GOUTIERES SYNDROME
Phase: PHASE2 • Sponsor: Adeline Vanderver, MD • Aim: Disease control
Last updated Jun 27, 2026 08:07 UTC
-
Could a single DNA test solve the mystery of rare brain diseases in kids?
Knowledge-focused CompletedThis study looked at whether whole genome sequencing (a complete read of a person's DNA) can help diagnose leukodystrophies, a group of rare brain diseases that are hard to identify. Researchers enrolled 236 children with white matter abnormalities on brain scans but no known gen…
Matched conditions: AICARDI GOUTIERES SYNDROME
Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated Jun 27, 2026 07:56 UTC