Cure My Disease

Don't miss your cure!

Log in / Sign up

Juvenile-onset Steinert myotonic dystrophy

MONDO:0035648

Also known as: Juvenile-onset Steinert disease, Juvenile-onset myotonic dystrophy type 1

7 clinical trials for this condition and its sub-types.

Follow this condition — get notified about new trials

Broader categories

Disease (680) Nervous system disorder (231) Musculoskeletal system disorder (207) Hereditary disease (176) Neuromuscular disease (106) Muscular dystrophy (72) Muscle tissue disorder (56) Myotonic dystrophy (55) Syndromic disease (25) Human disease (14)

Trials to join now! 6 Completed 1

Experimental drug tideglusib tested for rare muscle disease

Disease control Completed

This phase 2 study tested the safety and effectiveness of tideglusib, an experimental drug, in 16 adolescents and adults with congenital or juvenile-onset myotonic dystrophy type 1. Participants received either 400 mg or 1000 mg of tideglusib daily. The study measured side effect…

Phase: PHASE2 • Sponsor: AMO Pharma Limited • Aim: Disease control

Last updated Jun 26, 2026 16:48 UTC