Disease characteristic
MONDO:0021125An attribute of a disease.
Also known as: disease qualifier, modifier, qualifier
16 clinical trials for this condition and its sub-types.
Follow this condition to get notified about new trialsSub-types
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Hope for duchenne: new drug targets rare gene mutation in phase 3 trial
Disease control Recruiting nowThis study tests an experimental drug called AOC 1044 for boys with Duchenne muscular dystrophy (DMD) who have a specific genetic change (exon 44 skipping). About 70 boys aged 7 to 16 who can still walk will receive either the drug or a placebo. The main goal is to see if the dru…
Phase 3 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated Sep 09, 2026 15:00 UTC
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Donor immune cells show promise against dangerous viruses in vulnerable patients
Disease control Recruiting nowThis study tests whether specially grown immune cells from an unrelated donor can safely treat viral infections in people with weakened immune systems, such as after a stem cell transplant. About 750 participants will receive these cells and be monitored for side effects like inf…
Phase 2 • Sponsor: Children's Hospital Medical Center, Cincinnati • Aim: Disease control
Last updated Sep 06, 2026 00:00 UTC
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Experimental T-Cell therapy targets CMV in transplant patients
Disease control Recruiting nowThis study tests an experimental therapy that uses special immune cells (T-cells) from a donor to fight cytomegalovirus (CMV) infection in people who have had a stem cell transplant. The therapy aims to boost the patient's immune system to clear the infection. About 20 participan…
Early phase 1 • Sponsor: Mari Dallas • Aim: Disease control
Last updated Jun 27, 2026 07:55 UTC
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Why are some women with turner syndrome fertile? scientists launch genetic hunt
Knowledge-focused Recruiting nowThis study aims to create a large genetic database of people with Turner syndrome, a rare condition where a person is missing all or part of an X chromosome. Researchers want to compare the genes of women with Turner syndrome who are fertile with those who are not. Up to 500 part…
Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) • Aim: Knowledge-focused
Last updated Aug 08, 2026 00:03 UTC
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Blood test vs. scalpel: could liquid biopsy replace tissue biopsies for cancer monitoring?
Knowledge-focused Recruiting nowThis large observational study is testing whether a blood-based 'liquid biopsy' can detect tumor mutations and track disease progression in people with metastatic or advanced solid tumors who are receiving palliative care. Researchers will compare results from liquid biopsies wit…
Sponsor: University Hospital Augsburg • Aim: Knowledge-focused
Last updated Aug 01, 2026 00:00 UTC
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Where does the BK virus come from? new study aims to find out
Knowledge-focused Recruiting nowThis study looks at 100 kidney transplant patients to understand where the BK virus comes from and why some people get sicker than others. Researchers will compare the virus in patients and their donors, and check how the immune system responds. The goal is to find better ways to…
Sponsor: University Hospital, Grenoble • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:37 UTC
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Could your genes predict heart damage from irregular heartbeat?
Knowledge-focused Recruiting nowThis study investigates whether certain genetic variations make some people with atrial fibrillation more likely to develop a weakened heart muscle (cardiomyopathy). Researchers will compare the DNA of 299 participants, including those with AF-related cardiomyopathy and control g…
Sponsor: Barts & The London NHS Trust • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:31 UTC