New transplant approach aims to fix immune system in rare diseases
NCT ID NCT04232085
First seen Jan 04, 2026 · Last updated May 22, 2026 · Updated 21 times
Summary
This study tests a stem cell transplant using milder chemotherapy for people with certain immune deficiencies or bone marrow failure. The goal is to see if donor cells can take over the bone marrow and restore a working immune system. About 27 participants will be enrolled, and the main measure is whether donor cells make up at least 95% of blood cells by day 60.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
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Locations
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Johns Hopkins University
RECRUITINGBaltimore, Maryland, 21287, United States
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Contact Email: •••••@•••••
Conditions
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