Experimental stem cell infusions offered to single child with rare muscle disease
NCT ID NCT05154851
First seen Nov 01, 2025 · Last updated May 23, 2026 · Updated 28 times
Summary
This study provided an experimental stem cell treatment to one child with a rare form of congenital muscular dystrophy caused by a LMNA gene mutation. The child received 14 intravenous infusions of their own banked stem cells. The goal was to see if the treatment is safe and can help control the disease.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Hope Biosciences Stem Cell Research Foundation
Sugar Land, Texas, 77478, United States
Conditions
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