Experimental stem cells infused in rare muscle disease child
NCT ID NCT05154851
First seen Nov 01, 2025 · Last updated May 16, 2026 · Updated 27 times
Summary
This study gave 14 intravenous infusions of the patient's own banked stem cells to a single child with a rare, severe form of congenital muscular dystrophy caused by a LMNA gene mutation. The goal was to see if the treatment is safe and can help control the disease. Because the child had to have their own stem cells stored beforehand, this approach is only available to a very limited group.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Hope Biosciences Stem Cell Research Foundation
Sugar Land, Texas, 77478, United States
Conditions
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