Gene therapy for duchenne MD: Long-Term safety check begins
NCT ID NCT06491927
First seen Feb 26, 2026 · Last updated May 21, 2026 · Updated 11 times
Summary
This study follows 66 boys with Duchenne muscular dystrophy who already received RGX-202 gene therapy in an earlier trial. Researchers will monitor safety and track how well the therapy helps with muscle function over time, such as standing, walking, and climbing. The goal is to see if the treatment remains safe and effective in the long run.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for DUCHENNE MUSCULAR DYSTROPHY are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Locations
-
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
-
Arkansas Children's Hospital
Little Rock, Arkansas, 72202, United States
-
Stanford School of Medicine /Division of Neuromuscular Medicine
Palo Alto, California, 94304, United States
-
The University of Texas Southwestern Medical Center
Dallas, Texas, 75390, United States
-
Virginia Commonwealth University
Richmond, Virginia, 23298, United States
Conditions
Explore the condition pages connected to this study.