Gene therapy for duchenne MD: Long-Term safety and strength check
NCT ID NCT06491927
First seen Feb 26, 2026 · Last updated May 02, 2026 · Updated 8 times
Summary
This study follows 66 boys with Duchenne muscular dystrophy who previously received RGX-202 gene therapy in an earlier trial. Researchers will monitor safety and measure how well the therapy helps with standing, walking, and climbing over time. The goal is to see if the treatment remains safe and effective in the long run.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, 60611, United States
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Arkansas Children's Hospital
Little Rock, Arkansas, 72202, United States
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Stanford School of Medicine /Division of Neuromuscular Medicine
Palo Alto, California, 94304, United States
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The University of Texas Southwestern Medical Center
Dallas, Texas, 75390, United States
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Virginia Commonwealth University
Richmond, Virginia, 23298, United States
Conditions
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