Real-World data reveals how kids with spinal muscular atrophy are treated
NCT ID NCT07474311
First seen Mar 20, 2026 · Last updated May 25, 2026 · Updated 9 times
Summary
This study looked at medical records of 213 children with spinal muscular atrophy (SMA) in the Czech and Slovak Republics. Researchers wanted to see how treatments are actually used in real life and what health outcomes children experience. The goal was to learn more about care patterns, not to test a new treatment.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Novartis
Prague, 140 00, Czechia
Conditions
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