Doctors look back: how well do SMA treatments really work for kids?
NCT ID NCT07474311
Summary
This study aimed to understand how well the available treatments work for children with spinal muscular atrophy (SMA) in everyday life, not just in clinical trials. Researchers looked back at the medical records of 213 children in the Czech and Slovak Republics to see their treatment patterns, motor function, and overall health over time. The goal was to gather real-world evidence to help doctors make better treatment decisions.
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Contacts and locations
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Locations
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Novartis
Prague, 140 00, Czechia
Conditions
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