Testing a new drug for a rare, Life-Threatening childhood disease
NCT ID NCT07142343
Summary
This study is testing a drug called pozelimab in young children (1-5 years old) with a rare and serious genetic disease called CHAPLE. The main goal is to see if the drug is safe and well-tolerated in this young age group. Researchers will also check how the drug works in the body and if it helps improve certain protein levels in the blood.
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Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
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Genom att skicka in godkänner du våra Användarvillkor
Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Marmara University Hospital
RECRUITINGIstanbul, 10 34899, Turkey (Türkiye)
Conditions
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