New hope for DMD: Long-Term vamorolone safety tracked in 80 boys
NCT ID NCT06713135
First seen Dec 26, 2025 · Last updated May 22, 2026 · Updated 20 times
Summary
This study follows 80 boys with Duchenne muscular dystrophy who have already taken vamorolone in earlier studies. Researchers want to see how safe and effective the drug is over a longer period, especially regarding bone health and fractures. The goal is to better manage the disease and improve quality of life.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Alder Hey Children's Hospital
Liverpool, Merseyside, L14 5AB, United Kingdom
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Children's Health Ireland at Tallaght, Tallaght University Hospital
Dublin, D24TN3C, Ireland
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Children's Hospital Agia Sofia
Athens, 115 27, Greece
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Fakultni Nemocnice Motol
Prague, 150 06, Czechia
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Great Ormond Street Hospital for Children NHS Foundation Trust
London, WC1N 3JH, United Kingdom
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Hospital Universitario Puerta de Hierro Majadahonda
Madrid, 28222, Spain
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Hospital Universitario y Politecnico de La Fe
Valencia, 46026, Spain
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Leeds Teaching Hospitals NHS Trust
Leeds, West Yorkshire, LS1 3EX, United Kingdom
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Leiden University Medical Center
Leiden, 2333 ZA, Netherlands
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Queen Elizabeth University Hospital
Glasgow, Lanarkshire, United Kingdom
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Radboud University Nijmegen
Nijmegen, 6525 HB, Netherlands
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Schneider Children's Medical Center
Petah Tikva, 4920235, Israel
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Te Wao Nui - Child Health Service, Wellington Hospital
Wellington, 6021, New Zealand
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The John Walton Muscular Dystrophy Research Centre
Newcastle, NE1 3BZ, United Kingdom
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UZ Gent (Universitair Ziekenhuis Gent)
Ghent, 9000, Belgium
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UZ Leuven (Universitair Ziekenhuis Leuven)
Leuven, 3000, Belgium
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University Hospital Brno
Brno, Czechia
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University Hospitals Birmingham NHS Foundation Trust
Birmingham, B9 5SS, United Kingdom
Conditions
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