New PKU drug JNT-517 moves to Long-Term safety check in phase 3 trial
NCT ID NCT06628128
First seen Apr 29, 2026 · Last updated May 22, 2026 · Updated 2 times
Summary
This study tests the long-term safety of an experimental drug called JNT-517 for children and adults with phenylketonuria (PKU), a genetic condition that causes harmful buildup of phenylalanine. About 240 participants who completed earlier JNT-517 studies or are new to the drug will take JNT-517 and be monitored for side effects and changes in blood phenylalanine levels. The goal is to see if the drug is safe to use over time to help control the disease.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
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Locations
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Children's Health Queensland - Queensland Children's Hospital
RECRUITINGSouth Brisbane, Queensland, 4101, Australia
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Children's Medical Center Dallas
RECRUITINGDallas, Texas, 75235, United States
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Mater Health - Mater Hospital Brisbane
RECRUITINGSouth Brisbane, Queensland, 4101, Australia
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Murdoch Children's Research Institute
RECRUITINGParkville, Victoria, 3052, Australia
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Oregon Health and Science University
RECRUITINGPortland, Oregon, 97239, United States
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Royal Adelaide Hospital
RECRUITINGAdelaide, South Australia, 5000, Australia
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University of Florida (UF) Health Shands Hospital
RECRUITINGGainesville, Florida, 32608, United States
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University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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University of South Florida
RECRUITINGTampa, Florida, 33606, United States
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University of Texas Health (UTHealth) Science Center at Houston
RECRUITINGHouston, Texas, 77030, United States
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University of Texas Southwestern Medical Center
RECRUITINGDallas, Texas, 75390, United States
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Utah Health - The University of Utah Hospital
RECRUITINGSalt Lake City, Utah, 84112, United States
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Conditions
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