New PKU drug JNT-517 moves to Long-Term safety check in phase 3 trial

NCT ID NCT06628128

First seen Apr 29, 2026 · Last updated May 14, 2026 · Updated 1 time

Summary

This study tests the long-term safety of an experimental drug called JNT-517 in children and adults with PKU, a genetic condition that causes harmful buildup of phenylalanine. All 240 participants will receive the drug, and researchers will monitor side effects and changes in blood phenylalanine levels. The goal is to see if JNT-517 is safe enough for ongoing use to control the disease.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for PHENYLKETONURIA (PKU) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Health Queensland - Queensland Children's Hospital

    RECRUITING

    South Brisbane, Queensland, 4101, Australia

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Medical Center Dallas

    RECRUITING

    Dallas, Texas, 75235, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Mater Health - Mater Hospital Brisbane

    RECRUITING

    South Brisbane, Queensland, 4101, Australia

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Murdoch Children's Research Institute

    RECRUITING

    Parkville, Victoria, 3052, Australia

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Oregon Health and Science University

    RECRUITING

    Portland, Oregon, 97239, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Royal Adelaide Hospital

    RECRUITING

    Adelaide, South Australia, 5000, Australia

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Florida (UF) Health Shands Hospital

    RECRUITING

    Gainesville, Florida, 32608, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh

    RECRUITING

    Pittsburgh, Pennsylvania, 15224, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of South Florida

    RECRUITING

    Tampa, Florida, 33606, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Texas Health (UTHealth) Science Center at Houston

    RECRUITING

    Houston, Texas, 77030, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Texas Southwestern Medical Center

    RECRUITING

    Dallas, Texas, 75390, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Utah Health - The University of Utah Hospital

    RECRUITING

    Salt Lake City, Utah, 84112, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.