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Extended treatment trial for rare immune disease seeks to prove long-term safety

NCT ID NCT02859727

Summary

This study provided long-term treatment with the drug CDZ173 to patients with APDS/PASLI, a rare genetic immune disorder. The research followed 37 patients who had previously participated in related studies to monitor the drug's safety and effectiveness over time. The goal was to understand how well patients tolerated the medication and whether it continued to help manage their condition during extended use.

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Contacts and locations

Locations

  • Pharming Investigative Site

    Bethesda, Maryland, 20892, United States

  • Pharming Investigative Site

    Minsk, 223053, Belarus

  • Pharming Investigative Site

    Prague, CZE, 15006, Czechia

  • Pharming Investigative Site

    Dresden, 01307, Germany

  • Pharming Investigative Site

    Brescia, BS, 25123, Italy

  • Pharming Investigative Site

    Palermo, PA, 90127, Italy

  • Pharming Investigative Site

    Rotterdam, 3000 CA, Netherlands

  • Pharming Investigative Site

    Moscow, 117198, Russia

Conditions

Explore the condition pages connected to this study.