Extended treatment trial for rare immune disease halted

NCT ID NCT02859727

Summary

This study aimed to provide long-term treatment with CDZ173 to patients with APDS/PASLI, a rare genetic immune disorder. It followed patients who had previously participated in related studies to monitor the drug's safety and effectiveness over time. The study was terminated and involved 37 participants who continued taking the medication during the research period.

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Contacts and locations

Locations

  • Pharming Investigative Site

    Bethesda, Maryland, 20892, United States

  • Pharming Investigative Site

    Minsk, 223053, Belarus

  • Pharming Investigative Site

    Prague, CZE, 15006, Czechia

  • Pharming Investigative Site

    Dresden, 01307, Germany

  • Pharming Investigative Site

    Brescia, BS, 25123, Italy

  • Pharming Investigative Site

    Palermo, PA, 90127, Italy

  • Pharming Investigative Site

    Rotterdam, 3000 CA, Netherlands

  • Pharming Investigative Site

    Moscow, 117198, Russia

Conditions

Explore the condition pages connected to this study.