Gene therapy may free Beta-Thalassemia patients from lifelong transfusions
NCT ID NCT06308159
First seen Jan 04, 2026 · Last updated May 24, 2026 · Updated 23 times
Summary
This early-stage study tests a one-time gene therapy for people with a severe form of beta-thalassemia that requires regular blood transfusions. The treatment uses the patient's own blood stem cells, which are modified in a lab to produce healthy hemoglobin. The goal is to see if this therapy can raise hemoglobin levels enough to reduce or stop the need for transfusions. Six participants will be enrolled and followed for safety and effectiveness.
Disclaimer
Read more
Show less
This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for BETA-THALASSEMIA are added.
Genom att skicka in godkänner du våra Användarvillkor
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
Genom att skicka in godkänner du våra Användarvillkor
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
920th Hospital of Joint Logistics Support Force of People's Liberation Army of China
RECRUITINGKunming, Yunnan, 650100, China
Contact Email: •••••@•••••
-
Kunming Hope of Health Hospital
RECRUITINGKunming, Yunnan, 650200, China
Contact Email: •••••@•••••
Conditions
Explore the condition pages connected to this study.