Inhaled gene therapy aims to tackle cystic fibrosis from within
NCT ID NCT05248230
First seen Nov 15, 2025 · Last updated May 22, 2026 · Updated 27 times
Summary
This early-stage trial tests a single inhaled dose of a gene therapy called 4D-710 in 30 adults with cystic fibrosis who cannot use current modulator drugs. The goal is to see if the treatment is safe and tolerable. Researchers will monitor side effects and changes in lung function over time.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Boston Children's Hospital
RECRUITINGBoston, Massachusetts, 02115, United States
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Johns Hopkins Hospital
RECRUITINGBaltimore, Maryland, 21287, United States
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Massachusetts General Hospital
RECRUITINGBoston, Massachusetts, 02114, United States
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Medical University of South Carolina
RECRUITINGCharleston, South Carolina, 29425, United States
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National Jewish Health
RECRUITINGDenver, Colorado, 80206, United States
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Nationwide Children's Hospital
RECRUITINGColumbus, Ohio, 43205, United States
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Northwestern Memorial Hospital
RECRUITINGChicago, Illinois, 60611, United States
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Penn State Health
RECRUITINGHershey, Pennsylvania, 17033, United States
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Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center
RECRUITINGCleveland, Ohio, 44146, United States
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The Hospital of the University of Pennsylvania
RECRUITINGPhiladelphia, Pennsylvania, 19104, United States
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The University of Arizona
RECRUITINGTucson, Arizona, 85724, United States
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The University of Texas Southwestern Medical Center
RECRUITINGDallas, Texas, 75390, United States
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University of Alabama Child Health Research Unit
RECRUITINGBirmingham, Alabama, 35233, United States
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University of California San Francisco
RECRUITINGSan Francisco, California, 94143, United States
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University of Florida
RECRUITINGGainesville, Florida, 32610, United States
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University of Kansas Medical Center
RECRUITINGKansas City, Kansas, 66160, United States
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University of Miami Hospital
RECRUITINGMiami, Florida, 33136, United States
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University of North Carolina at Chapel Hill
COMPLETEDChapel Hill, North Carolina, 27599, United States
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University of Washington Medical Center
RECRUITINGSeattle, Washington, 98195, United States
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Virginia Commonwealth University Health System
RECRUITINGRichmond, Virginia, 23298, United States
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Conditions
Explore the condition pages connected to this study.