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New gene therapy hopes to tame rare copper disorder

NCT ID NCT07173933

First seen Nov 01, 2025 · Last updated May 20, 2026 · Updated 27 times

Summary

This early-stage trial tests a gene therapy called GC310 for Wilson's disease, a rare condition where copper builds up in the body. About 15 adults will receive a single dose and be followed for a year to check safety and how well it works. The goal is to see if the therapy can help the body manage copper levels and improve liver and nerve symptoms.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Peking Union Medical College

    Beijing, 100005, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

    Contact

Conditions

Explore the condition pages connected to this study.