New drug trial targets root cause of rare Muscle-Wasting disease
NCT ID NCT06131983
Summary
This early-stage study is testing a new drug called ARO-DUX4 in adults and adolescents with FSHD1, a genetic muscle-wasting disease. The main goals are to see if the drug is safe, how the body processes it, and if it affects the target in the muscle. Participants will receive the drug or a placebo and undergo muscle biopsies to measure any changes.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Research Site
WITHDRAWNBangkok, 10700, Thailand
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Research Site 1
RECRUITINGBirtinya, Queensland, 4575, Australia
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Research Site 1
RECRUITINGMontreal, Quebec, H3A2B4, Canada
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Research Site 1
RECRUITINGUlm, 89081, Germany
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Research Site 1
RECRUITINGMilan, 20162, Italy
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Research Site 1
RECRUITINGLeiden, 2333, Netherlands
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Research Site 1
RECRUITINGAuckland, 1010, New Zealand
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Research Site 1
RECRUITINGValencia, 46026, Spain
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Research Site 2
RECRUITINGLiverpool, New South Wales, 2170, Australia
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Research Site 2
NOT_YET_RECRUITINGCalgary, Alberta, T2N4Z6, Canada
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Research Site 2
RECRUITINGMünchen, 80336, Germany
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Research Site 2
RECRUITINGRoma, 00168, Italy
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Research Site 2
RECRUITINGMadrid, 28034, Spain
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Research Site 3
RECRUITINGAuchenflower, Queensland, 4066, Australia
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Research Site 3
RECRUITINGEdmonton, Alberta, T6G2G4, Canada
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Research Site 3
RECRUITINGBarcelona, 08035, Spain
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Research Site 4
RECRUITINGMelbourne, Victoria, 3004, Australia
Conditions
Explore the condition pages connected to this study.