Stem cell hope for rare brain disease: new trial tracks Real-World impact
NCT ID NCT04503213
First seen Oct 31, 2025 · Last updated Apr 29, 2026 · Updated 28 times
Summary
This study follows 20 adults with CSF1R-related leukoencephalopathy, a rare genetic brain disease, to see if a stem cell transplant can stabilize or improve thinking and movement. Researchers will track changes over time using exams and brain scans. The goal is to understand if this treatment can control the disease long-term.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Locations
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Mayo Clinic in Florida
Jacksonville, Florida, 32224, United States
Conditions
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