Cystic fibrosis gene repair shows promise in lab, study halted early
NCT ID NCT05100823
First seen Nov 01, 2025 · Last updated May 22, 2026 · Updated 28 times
Summary
This study aimed to see if special molecules called oligonucleotide blockers could fix a common genetic problem in cystic fibrosis. Researchers took cells from 16 patients with CFTR gene mutations and tested the blockers in the lab. The goal was to restore the missing protein and improve cell function. The study was terminated early, so results are limited.
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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Montpellier University Hospital
Montpellier, 34090, France
Conditions
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