Taysha Gene Therapies, Inc.
Clinical trials sponsored by Taysha Gene Therapies, Inc., explained in plain language.
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One-Time gene shot could change lives of rett syndrome patients
Disease control Recruiting nowThis study tests a one-time gene therapy called TSHA-102 for females with Rett syndrome, a severe genetic disorder. The therapy is given as a single injection into the spine. The goal is to see if it is safe and can help patients regain lost skills like walking or talking. The st…
Phase: PHASE3 • Sponsor: Taysha Gene Therapies, Inc. • Aim: Disease control
Last updated May 26, 2026 11:26 UTC
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Gene therapy hope for toddlers with rare brain disorder
Disease control Recruiting nowThis study tests a one-time gene therapy called TSHA-102 in girls aged 2 to 4 with Rett syndrome, a severe genetic brain disorder. The treatment is given as a single injection into the spinal fluid. The goal is to see if it is safe and if it can improve symptoms. Only 3 participa…
Phase: PHASE3 • Sponsor: Taysha Gene Therapies, Inc. • Aim: Disease control
Last updated May 26, 2026 11:08 UTC