Taysha Gene Therapies, Inc.
Clinical trials sponsored by Taysha Gene Therapies, Inc., explained in plain language.
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Gene therapy hope for toddlers with rett syndrome
Disease control Recruiting nowThis study tests a one-time gene therapy called TSHA-102 in girls aged 2 to 4 with Rett syndrome, a severe genetic disorder. The therapy is given as a single injection into the spine. The main goal is to check if it is safe and tolerable, and to see early signs of whether it help…
Phase: PHASE3 • Sponsor: Taysha Gene Therapies, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:37 UTC
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New gene therapy hopes to restore milestones in rett syndrome
Disease control Recruiting nowThis study tests a one-time gene therapy called TSHA-102 in females aged 6 to under 22 with classic Rett syndrome. The goal is to see if it is safe and can help them regain or gain new developmental skills like walking or talking. Participants receive the therapy through a spinal…
Phase: PHASE3 • Sponsor: Taysha Gene Therapies, Inc. • Aim: Disease control
Last updated Jun 27, 2026 08:07 UTC