Shire

This study tests a medicine called SHP611, given as a shot into the fluid around the spine, for children with late infantile metachromatic leukodystrophy (MLD), a rare and serious brain disease. The main goal is to see if it helps children keep the ability to walk and move for lo…

This study is a worldwide registry that follows people with short bowel syndrome over many years to see how safe the drug teduglutide is and how their health changes over time. It includes both people who take teduglutide and those who do not. The goal is to better understand lon…