Prime Medicine, Inc.
Clinical trials sponsored by Prime Medicine, Inc., explained in plain language.
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Groundbreaking gene therapy aims to fix immune system in rare disease
Disease control ENROLLING_BY_INVITATIONThis study tests a new gene therapy called PM359 for people with a rare immune disorder called chronic granulomatous disease (CGD). The therapy takes the patient's own blood stem cells, fixes a specific gene mutation using a precise editing tool called prime editing, and then ret…
Phase: PHASE1, PHASE2 • Sponsor: Prime Medicine, Inc. • Aim: Disease control
Last updated May 26, 2026 09:03 UTC
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Researchers seek wilson disease patients to shape future gene editing trials
Knowledge-focused OngoingThis study aims to better understand how people with Wilson disease manage their condition and what influences their decision to join clinical research. About 30 adults with confirmed Wilson disease will complete surveys about their symptoms, treatments, diet, and interest in a f…
Sponsor: Prime Medicine, Inc. • Aim: Knowledge-focused
Last updated May 26, 2026 08:33 UTC