Pharming Technologies
Clinical trials sponsored by Pharming Technologies, explained in plain language.
A biopharmaceutical company developing treatments for rare diseases.
Not investment advice. Company information is shown for context only. Clinical trials frequently fail.
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Upcoming readouts
Trials from this sponsor expected to report results within the next 12 months.
- New drug aims to calm overactive immune system in rare disorders Results expected Nov 2026 (estimated)
- New hope for kids with rare immune disease: drug targets root cause Results expected Nov 2026 (estimated) 🚀 Make-or-break
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New pill aims to ease fatigue in rare mitochondrial disease
Disease control Recruiting nowThis study is for people who completed a previous trial of KL1333 (napazimone) for primary mitochondrial disease. It will test the drug's long-term safety and whether it helps with fatigue and daily activities. About 140 participants will take the pill twice daily for an extended…
Phase 2 • Sponsor: Pharming Technologies B.V. • Aim: Disease control
Last updated Sep 18, 2026 00:00 UTC
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New drug aims to ease fatigue in mitochondrial disease
Symptom relief Recruiting nowThis Phase 2 trial tests whether KL1333 can reduce fatigue and improve leg strength in adults with primary mitochondrial disease, a genetic condition that affects energy production. About 180 participants will receive either KL1333 or a placebo twice daily for 48 weeks. The study…
Phase 2 • Sponsor: Pharming Technologies B.V. • Aim: Symptom relief
Last updated Jun 28, 2026 00:00 UTC