Intrabio Inc
Clinical trials sponsored by Intrabio Inc, explained in plain language.
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New hope for rare disease: expanded access to experimental drug for A-T patients
Disease control AVAILABLEThis program provides an experimental drug, levacetylleucine, to people with Ataxia-Telangiectasia (A-T), a rare and serious genetic disease that affects movement and immune function. It is for patients who cannot join clinical trials and have no other good treatment options. The…
Sponsor: IntraBio Inc • Aim: Disease control
Last updated May 26, 2026 10:02 UTC
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Hope for rare brain disease: new drug trial targets movement and daily life
Disease control Recruiting nowThis study tests an experimental drug called N-acetyl-L-leucine (IB1001) for people aged 4 and older with Niemann-Pick disease type C (NPC), a rare genetic disorder that affects movement and thinking. About 53 participants will receive either the drug or a placebo for a period, t…
Phase: PHASE3 • Sponsor: IntraBio Inc • Aim: Disease control
Last updated May 26, 2026 08:19 UTC