Insmed Gene Therapy Llc
Clinical trials sponsored by Insmed Gene Therapy Llc, explained in plain language.
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Gene therapy injection hopes to slow ALS
Disease control Recruiting nowThis early-stage study tests a single injection of a gene therapy called INS1202 for people with ALS, a disease that weakens muscles over time. The main goal is to see if it is safe and to find the best dose. About 23 adults with certain genetic types of ALS will take part.
Phase: PHASE1 • Sponsor: Insmed Gene Therapy LLC • Aim: Disease control
Last updated May 19, 2026 11:47 UTC
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Gene therapy hope for toddlers with duchenne muscular dystrophy
Disease control Recruiting nowThis early-stage study tests a single injection of a gene therapy called INS1201 in 12 young boys (ages 2 to 5) with Duchenne muscular dystrophy who can still walk. The main goal is to see if the treatment is safe and where it goes in the body. Researchers will also look for sign…
Phase: PHASE1 • Sponsor: Insmed Gene Therapy LLC • Aim: Disease control
Last updated May 15, 2026 11:54 UTC