Guangzhou Women And Children's Medical Center

This early-phase study tests a single dose of a gene therapy called YOLT-204 in 3 to 18 children and teens with severe beta-thalassemia or sickle cell disease. The goal is to see if it is safe and can raise fetal hemoglobin levels, which may reduce or eliminate the need for blood…

This study aims to create a dynamic early warning system for necrotizing enterocolitis (NEC), a severe gut emergency in preterm infants. Researchers will analyze genetic and immune markers from over 1,000 babies born before 32 weeks to better predict who is at highest risk. The g…