Guangzhou Women And Children's Medical Center

This early-stage study tests a single dose of a gene therapy called YOLT-204 in 18 children (ages 3-17) with severe beta-thalassemia or sickle cell disease. The goal is to see if it is safe and can raise fetal hemoglobin levels enough to reduce or stop the need for regular blood …

This study aims to create a smarter early warning system for necrotizing enterocolitis (NEC), a severe gut emergency in premature infants. Researchers will combine genetic information with routine blood test results to better predict which babies are at highest risk. The study wi…